Project information

Duchenne Muscular Dystrophy Research

We need £20,000 for a project at Oxford University that will research potential new drugs that could treat Duchenne Muscular Dystrophy.

We are asking for an early Christmas present this year – you make a donation to Duchenne Childrens’ Trust and WE get it doubled through the Christmas Challenge.

Two years

Charity information: The Duchenne Children's Trust

The Duchenne Children's Trust logo
  • Need

    Need

    This is an exciting project to look for drugs that will increase utrophin in the body.

    Boys with Duchenne Muscular Dystrophy are missing a protein called dystrophin, which is crucial for muscle survival. Utrophin is a protein that acts in the same way as dystrophin.

    This project will help to fund world-class scientific research at Oxford University and will help us to achieve our goal, to End Duchenne in Ten.

    Solution

    Dame Professor Kay Davies has been working on this treatment approach for many years and one of her drugs is about to go into a clinical trial.

    This project will look at new models to see if they are more potent and effective.They have already developed an advance screening programme to pick out these compounds.

    The project will run 24 months and the £20,000 we raise through the Christmas Challenge will help to fund the research.

  • Aims

    Aim 1

    We need £20,000 to spend on a project to look for drugs that will increase utrophin in the body

    Activities

    » We will co-fund the new utrophin research project led by Dame Professor Kay Davies at Oxford University

    We aim to exceed our fundraising total of £20,000 to help achieve our goals


  • Impact

    Impact

    Utrophin is a protein that acts in the same way as dystrophin, which boys with Duchenne Muscular Dystrophy lack. Without dystrophin, muscles die. Our project will fund research by Dame Professor Kay Davies at Oxford University into drugs that could increase utrophin levels.

    Risk

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    Reporting

    We communicate regularly with our followers through our Facebook and Twitter profiles and update them on all of our recent news and successes. Our own website is regularly updated with upcoming events and photos and videos of previous fundraisers.

  • Budget

    Budget - Project Cost: £20,000

    Loading graph....
      Amount Heading Description
      £20,000 Funding medical research Funding an Oxford University project that will look for drugs that increase utrophin in the body

    Current Funding / Pledges

    Source Amount
    M Crossley £5,000 Guaranteed
  • Background

    Location

    The research will take place at Oxford University under the leadership of Professor Dame Kay Davies, an international leader in Duchenne Muscular Dystrophy research.

    Beneficiaries

    Children with Duchenne Muscular Dystrophy and their families

  • Why Us?

    Why Us?

    We have successfully reached our fundraising target over the last year and hosted consistently successful fundraising events. We have also gained high levels of media coverage, including a recent appearance on BBC Radio 5 Live, raising awareness of the disease.

    Read more about the Charity running this project.

    People

    Emily Crossley

    Director and co-founder

    Nick Crossley

    Co-founder

    Patrick McKenna

    Policy adviser

Duchenne CT founder Emily with her son, Eli

Duchenne CT founder Emily with her son, Eli