Project information

Potential therapies to alleviate symptoms of A-T

To support through medical research the investigation of potential therapies that will help children who have the condition Ataxia-Telangiectasia (A-T)

Usually 12 - 24 months

Charity information: Action For A-T

Action For A-T logo
  • Need

    Need

    Ataxia-Telangiectasia (A-T) is a condition which affects children and young adults. Babies are born 'normal' and then slowly from 4 they begin to lose their independence often needing a wheelchair by 7 and a feeding tube by age 12. People with the condition have very weak immune systems and often dies in their teens or early twenties of cancer or a severe respiratory infection. There is currently no cure for this condition, no treatment and no way to halt the progression.

    Solution

    Action for A-T is working with researchers globally to advance understanding and knowledge of A-T with the aim of finding a treatment or potential therapy to make a difference to lives of people with A-T. These are more promising times for A-T children but research can only move at the pace that funds will allow. We are currently looking for funding to put into a project that is looking at developing a drug compound that could help not only people with A-T but also other neurological conditions.

  • Aims

    Aim 1

    To develop a drug that will help alleviate some or all of the symptoms associated with A-T.

    Activities

    » Work with researchers around the globe who are already working to advance this aim but who need further funding.

    There will be a project output that can be shared with other researchers which will help to advance knowledge.


  • Impact

    Impact

    Long term it will provide a treament for children and young adults with A-T. This can be demonstrated easily as there is currently nothing on the market for the condition.

    Risk

    Medical reserach involves a certain amount of trial and error. However there is no such thing as bad research as even where there is an apparent dead end in research this knowledge can be useful for further projects.

    Reporting

    There will be an end of project report and findings can also be shared on our website in brief.

  • Budget

    Budget - Project Cost: £100,000

    Loading graph....
      Amount Heading Description
      £100,000 Medical research project Running a 24 month research project
  • Background

    Location

    Action for A-T funds projects all around the globe and we have current projects in the UK, USA, Australia and Europe

    Beneficiaries

    Children and young adults with A-T

  • Why Us?

    Why Us?

    Because we are the only UK charity who's only remit is to advance medical research for A-T.

    Read more about the Charity running this project.

    People

    Sean Kelly

    Chief Executive